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GP

Gerard Platenburg

Chief Scientific Officer

ProQR

ProQR Pipeline

DrugIndicationPhase
QR-4210 (sepofarsen)Usher syndrome type 2A / Retinitis Pigmentosa (USH2A exon 13 mutations)Phase 2/3
QR-1123Autosomal Dominant Retinitis Pigmentosa (adRP) caused by P23H mutation in RHO genePhase 1/2
QR-504aFuchs Endothelial Corneal Dystrophy (FECD)Preclinical
Axiomer® Liver Candidate(s)Undisclosed genetic liver disordersDiscovery/Preclinical
Axiomer® CNS Candidate(s)Undisclosed genetic CNS disordersDiscovery/Preclinical