DC
Dr. Cristina Lopez Lopez, MD, PhD
Chief Medical Officer
ProQRProQR Pipeline
| Drug | Indication | Phase |
|---|
| AX-0810 | Rhodopsin-associated Autosomal Dominant Retinitis Pigmentosa (RHO-adRP) | Phase 1/2 |
| AX-1416 | Undisclosed Ophthalmic Target | Preclinical |
| AX-1501 | Undisclosed Ophthalmic Target | Preclinical |
| QR-4210 | Usher Syndrome (USH2A exon 13 mutations) | Phase 2/3 |