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Fabrice Chouraqui

Chief Executive Officer & Executive Director

Pharming Group

Pharming Group Pipeline

DrugIndicationPhase
Joenja® (leniolisib)Activated PI3K Delta Syndrome (APDS)Approved
PH-1 (Recombinant Human C1 Esterase Inhibitor)Primary Mitochondrial Diseases (e.g., Leigh Syndrome, MELAS)Pivotal