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EH

Ellen Hukkelhoven, Ph.D.

Board Member

MeiraGTx

MeiraGTx Pipeline

DrugIndicationPhase
AAV2-hAQP1Grade 2/3 Radiation-Induced Xerostomia (RIX)Phase 3
AAV-RPGRX-Linked Retinitis Pigmentosa (XLRP)Phase 3
AAV-CNGB3Achromatopsia (CNGB3-related)Phase 3
AAV-CNGA3Achromatopsia (CNGA3-related)Phase 3
AAV-GADParkinson's DiseasePhase 2
Riboswitch Platform (e.g., GLP-1)Obesity/DiabetesPreclinical/Research
Riboswitch Platform (CAR-T)Oncology / AutoimmunePreclinical/Research