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Charles W. Wagner, Jr.

Executive Vice President and Chief Financial Officer

Vertex Pharmaceuticals

Vertex Pharmaceuticals Pipeline

DrugIndicationPhase
Vanzacaftor/Tezacaftor/DeutivacaftorCystic FibrosisPhase 3
Exagamglogene Autotemcel (CASGEVY)Sickle Cell DiseaseApproved
VX-548Acute PainPhase 3
VX-880 / VP-102Type 1 DiabetesPhase 1/2
VX-407Alpha-1 Antitrypsin DeficiencyPhase 2
VX-670APOL1-Mediated Kidney DiseasePhase 2
VX-522Cystic FibrosisPhase 1/2