VX-407

About Vertex Pharmaceuticals

Vertex Pharmaceuticals has established itself as a premier, fully integrated biopharmaceutical company with a mission to discover, develop, and commercialize innovative medicines for serious diseases. Its landmark achievement is the creation of a portfolio of CFTR modulators that treat the underlying cause of cystic fibrosis for the majority of patients, generating multi-billion dollar annual revenues. The company's strategy is to reinvest these profits to expand its therapeutic reach through a deep pipeline of 264 candidates, utilizing advanced platforms in gene editing, cell therapy, and precision medicine to address adjacent markets with significant unmet medical need.

Therapeutic Areas

Other Alpha-1 Antitrypsin Deficiency Drugs