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AS

Amy Simon, M.D.

Chief Medical Officer

Beam Therapeutics

Beam Therapeutics Pipeline

DrugIndicationPhase
BEAM-101Sickle Cell Disease / Beta-ThalassemiaPhase 1/2
BEAM-102Sickle Cell DiseasePreclinical
BEAM-201Acute Myeloid Leukemia / R/R T-ALLPhase 1/2
BEAM-301Glycogen Storage Disease Type Ia (GSDIa)Preclinical
BEAM-302Alpha-1 Antitrypsin Deficiency (AATD)Phase 1/2