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SMA ASO Candidates

Spinal Muscular Atrophy

Discovery/PreclinicalActiveN/A

Key Facts

Indication
Spinal Muscular Atrophy
Phase
Discovery/Preclinical
Status
Active
Company

About Biogen

Founded in 1978, Biogen has established itself as a cornerstone of the biotechnology industry, renowned for pioneering multiple sclerosis treatments and launching the first approved therapy for Alzheimer's disease. The company's strategy is anchored in a focused R&D engine that reinvests approximately $2 billion annually into neurology, immunology, and rare disease pipelines, balancing bold scientific risk with disciplined capital allocation. Its mission is to translate cutting-edge science into transformative medicines, creating value for patients, shareholders, and communities.

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Other Spinal Muscular Atrophy Drugs

DrugCompanyPhase
Spinal Muscular Atrophy (Skeletal Muscle)MyoceaResearch
Evrysdi (Risdiplam)RocheApproved