HSC-GT for MPS-I

About Kyowa Kirin

Kyowa Kirin is a global specialty pharmaceutical leader with a mission to deliver 'life-changing value' by addressing high unmet medical needs through innovative antibody and gene therapies. The company has successfully transitioned into a global player, deriving 72% of its sales from international markets and maintaining a robust pipeline of 18 development programs. Its strategy is anchored in proprietary technology platforms like POTELLIGENT, strategic acquisitions such as Orchard Therapeutics, and a focused therapeutic approach in bone & mineral, hematologic, and rare diseases to drive sustainable growth towards its Vision 2030.

Therapeutic Areas