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CMP-002

SYNGAP1-related disorder

PreclinicalGLP tox studies ongoing

Key Facts

Indication
SYNGAP1-related disorder
Phase
Preclinical
Status
GLP tox studies ongoing
Company

About CAMP4 Therapeutics

CAMP4 Therapeutics is a clinical-stage biotech company developing first-in-class antisense oligonucleotide (ASO) therapeutics that upregulate gene expression by targeting regulatory RNA. The company has established a proprietary RAP Platform® to map gene-regulatory circuits and has advanced its lead program, CMP-001 for urea cycle disorders, into Phase 1/2 clinical development. CAMP4's strategy leverages its platform to build a pipeline in CNS and metabolic diseases while seeking strategic partnerships to expand its reach. The company is publicly traded and led by a team with deep expertise in RNA biology, drug development, and corporate strategy.

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