aTyr Pharma

aTyr Pharma

ATYRPhase 2
San Diego, United StatesFounded 2007atyrpharma.com

aTyr Pharma is translating the biology of tRNA synthetases, essential enzymes with newly discovered extracellular signaling functions, into first-in-class medicines for fibrosis and inflammation. The company's lead asset, efzofitimod, has demonstrated proof-of-concept in pulmonary sarcoidosis and is being advanced in a pivotal Phase 3 trial, with a parallel Phase 2 program in SSc-ILD. Through its subsidiary Pangu BioPharma in Hong Kong, aTyr is also exploring bispecific antibodies targeting Neuropilin-2 (NRP2) in oncology, expanding its platform's therapeutic reach.

Market Cap
$79.3M
-76.8% period
Pipeline
8
drug candidates
Patents
Publications

ATYR · Stock Price

USD 0.812.68 (-76.84%)

Historical price data

AI Company Overview

aTyr Pharma is translating the biology of tRNA synthetases, essential enzymes with newly discovered extracellular signaling functions, into first-in-class medicines for fibrosis and inflammation. The company's lead asset, efzofitimod, has demonstrated proof-of-concept in pulmonary sarcoidosis and is being advanced in a pivotal Phase 3 trial, with a parallel Phase 2 program in SSc-ILD. Through its subsidiary Pangu BioPharma in Hong Kong, aTyr is also exploring bispecific antibodies targeting Neuropilin-2 (NRP2) in oncology, expanding its platform's therapeutic reach.

Pulmonary & RespiratoryAutoimmune & InflammationFibrosisOncology

Technology Platform

Platform based on extracellular tRNA synthetase biology, leveraging naturally occurring immunomodulatory protein fragments to develop therapies for inflammation and fibrosis.

Pipeline

8
8 drugs in pipeline
DrugIndicationStageWatch
Efzofitimod 1 mg/kg + Efzofitimod 3 mg/kg + PlaceboSARS-CoV-2 (COVID-19) Severe PneumoniaPhase 2
efzofitimod 450 mg + efzofitimod 270 mg + PlaceboInterstitial Lung DiseasePhase 2
Efzofitimod 1.0 mg/kg or Placebo + Efzofitimod 3.0 mg/kg or ...Pulmonary SarcoidosisPhase 1/2
ATYR1940Facioscapulohumeral Muscular Dystrophy (FSHD)Phase 1/2
Placebo + ATYR1940Facioscapulohumeral Muscular Dystrophy (FSHD)Phase 1/2

Funding History

5
Total raised:$233M
PIPE$40MDec 15, 2020
IPO$60MJun 26, 2015
Series C$60MJun 15, 2014
Series B$51MJun 15, 2010

Opportunities

Efzofitimod has blockbuster potential in pulmonary sarcoidosis and SSc-ILD as a first-in-class, targeted immunomodulator.
Success could validate the tRNA synthetase platform, enabling expansion into other fibrotic and autoimmune diseases.
The Pangu bispecific antibody program represents a long-term opportunity in the large oncology market.

Risk Factors

High binary risk on upcoming Phase 3 data readout for efzofitimod in pulmonary sarcoidosis.
As a pre-revenue company, aTyr is dependent on capital markets for funding, facing dilution risk.
The novel mechanism, while differentiating, carries unproven clinical validation and potential unknown safety issues.

Competitive Landscape

In pulmonary sarcoidosis, competes against generic corticosteroids and immunosuppressants; key differentiation is targeted mechanism and steroid-sparing potential. In SSc-ILD, faces competition from approved therapies nintedanib and tocilizumab. The Pangu oncology program would enter a crowded bispecific antibody field but with a novel target in NRP2.