vosoritide

Phase 2Active
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49
Hype Score

Development Stage

Pre-clinical
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Achondroplasia

Conditions

Achondroplasia

Trial Timeline

Oct 10, 2020 → Dec 1, 2027

About vosoritide

vosoritide is a phase 2 stage product being developed by BioMarin Pharmaceutical for Achondroplasia. The current trial status is active. This product is registered under clinical trial identifier NCT04554940. Target conditions include Achondroplasia.

Hype Score Breakdown

Clinical
17
Activity
12
Company
7
Novelty
5
Community
5

Clinical Trials (2)

NCT IDPhaseStatus
NCT07073014Phase 3Recruiting
NCT04554940Phase 2Active

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49
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49
BMN 111 + Normal SalineBioMarin PharmaceuticalPhase 1
30
BMN 111BioMarin PharmaceuticalPhase 2
49
BMN 111 + PlaceboBioMarin PharmaceuticalPhase 2
49
BMN 111 administration via vial and syringeBioMarin PharmaceuticalPhase 1
30
Active BMN 111: Subcutaneous injection of recommended dose of BMN 111 based on weight-band dosing once daily.BioMarin PharmaceuticalPhase 2
49
BMN 111BioMarin PharmaceuticalPhase 2
49
BMN 111 + PlaceboBioMarin PharmaceuticalPhase 3
74
BMN 333 + Vosoritide Injection [Voxzogo]BioMarin PharmaceuticalPhase 2/3
62
BMN 111BioMarin PharmaceuticalPhase 3
74
TYRA-300 0.125 mg/kg + TYRA-300 0.25 mg/kg + TYRA-300 0.375 mg/kg + TYRA-300 0.50 mg/kgTyra BiosciencesPhase 2
47