UX007 + Placebo

Phase 3Terminated
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Interest: 26/100
26
Hype Score

Development Stage

Pre-clinical
Phase 1
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Glucose Transporter Type 1 Deficiency Syndrome (Glut1 DS)

Conditions

Glucose Transporter Type 1 Deficiency Syndrome (Glut1 DS)

Trial Timeline

Apr 19, 2017 → Oct 9, 2019

About UX007 + Placebo

UX007 + Placebo is a phase 3 stage product being developed by Ultragenyx Pharmaceutical for Glucose Transporter Type 1 Deficiency Syndrome (Glut1 DS). The current trial status is terminated. This product is registered under clinical trial identifier NCT02960217. Target conditions include Glucose Transporter Type 1 Deficiency Syndrome (Glut1 DS).

What happened to similar drugs?

4 of 5 similar drugs in Glucose Transporter Type 1 Deficiency Syndrome (Glut1 DS) were approved

Approved (4) Terminated (2) Active (1)
Exenatide + MetforminEli LillyApproved
Candesartan + PlaceboAstraZenecaApproved
cyclosporine micro-emulsionNovartisApproved
🔄Ramipril + RosiglitazonePfizerPhase 3

Hype Score Breakdown

Clinical
17
Activity
0
Company
9
Novelty
0
Community
0

Clinical Trials (2)

NCT IDPhaseStatus
NCT02960217Phase 3Terminated
NCT01993186Phase 2Completed

Competing Products

17 competing products in Glucose Transporter Type 1 Deficiency Syndrome (Glut1 DS)

See all competitors
ProductCompanyStageHype Score
Aspirin + Alpha lipoic acid + Olmesartan + PlaceboDaiichi SankyoPre-clinical
26
Exenatide + MetforminEli LillyApproved
43
AZD1656AstraZenecaPhase 1
29
Candesartan + PlaceboAstraZenecaApproved
35
Placebo for Sitagliptin 25 mg + Placebo for Sitagliptin 50 mg + Sitagliptin 25 mg + Sitagliptin 50 mgMerckPhase 2
35
Sitagliptin-Metformin + Metformin + Placebo pillMerckApproved
43
Comparator: exenatide + Comparator: exenatide + Comparator: PlaceboMerckPhase 1
29
Placebo + JanuviaMerckPhase 2
27
cyclosporine micro-emulsionNovartisApproved
35
Ramipril + RosiglitazonePfizerPhase 3
40
HSK7653 10mg Q2W + HSK7653 25mg Q2W + PlaceboHaisco Pharmaceutical GroupPhase 2
35
TriheptanoinUltragenyx PharmaceuticalPre-clinical
20
UX007Ultragenyx PharmaceuticalPhase 2
21
TriheptanoinUltragenyx PharmaceuticalPhase 2
25
TriheptanoinUltragenyx PharmaceuticalPhase 2
29
UX007 + PlaceboUltragenyx PharmaceuticalPhase 2
29
GFT505 80mg + PlaceboGenfitPhase 2
25