Sodium phenylbutyrate

Phase 1Recruiting
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25
Hype Score

Development Stage

βœ“
Pre-clinical
2
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Combined D,L-2-hydroxyglutaric Aciduria

Conditions

Combined D,L-2-hydroxyglutaric Aciduria

Trial Timeline

Jul 30, 2025 β†’ Dec 1, 2027

About Sodium phenylbutyrate

Sodium phenylbutyrate is a phase 1 stage product being developed by Zevra Therapeutics for Combined D,L-2-hydroxyglutaric Aciduria. The current trial status is recruiting. This product is registered under clinical trial identifier NCT07125066. Target conditions include Combined D,L-2-hydroxyglutaric Aciduria.

Hype Score Breakdown

Clinical
10
Activity
5
Company
2
Novelty
3
Community
2

Clinical Trials (2)

NCT IDPhaseStatus
NCT07125066Phase 1Recruiting
NCT06773026Phase 2Recruiting

Competing Products

6 competing products in Combined D,L-2-hydroxyglutaric Aciduria

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Vaxelisβ„’MerckApproved
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Leios/AlessePfizerPre-clinical
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