Sapropterin (Kuvan)

Pre-clinicalCompleted
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20
Hype Score

Development Stage

1
Pre-clinical
2
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Phenylketonuria

Conditions

Phenylketonuria

Trial Timeline

Jul 1, 2008 โ†’ May 1, 2018

About Sapropterin (Kuvan)

Sapropterin (Kuvan) is a pre-clinical stage product being developed by BioMarin Pharmaceutical for Phenylketonuria. The current trial status is completed. This product is registered under clinical trial identifier NCT00730080. Target conditions include Phenylketonuria.

Hype Score Breakdown

Clinical
5
Activity
2
Company
7
Novelty
2
Community
1

Clinical Trials (1)

NCT IDPhaseStatus
NCT00730080Pre-clinicalCompleted

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