QR-421a

Phase 1/2Completed
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Interest: 22/100
22
Hype Score

Development Stage

Pre-clinical
2
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Retinitis Pigmentosa

Conditions

Retinitis Pigmentosa, Usher Syndrome Type 2, Deaf Blind, Retinal Disease, Eye Diseases, Eye Diseases, Hereditary, Eye Disorders Congenital, Vision Disorders

Trial Timeline

Mar 6, 2019 → Oct 14, 2021

About QR-421a

QR-421a is a phase 1/2 stage product being developed by ProQR for Retinitis Pigmentosa. The current trial status is completed. This product is registered under clinical trial identifier NCT03780257. Target conditions include Retinitis Pigmentosa, Usher Syndrome Type 2, Deaf Blind.

What happened to similar drugs?

0 of 3 similar drugs in Retinitis Pigmentosa were approved

Approved (0) Terminated (0) Active (3)
🔄GanciclovirRochePhase 3
🔄ValganciclovirRochePhase 3

Hype Score Breakdown

Clinical
9
Activity
8
Company
5
Novelty
0
Community
0

Clinical Trials (1)

NCT IDPhaseStatus
NCT03780257Phase 1/2Completed

Competing Products

20 competing products in Retinitis Pigmentosa

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ProductCompanyStageHype Score
DSP-3077 Retinal Sheet Cohort 1 + DSP-3077 Retinal Sheet Cohort 2 + DSP-3077 Retinal Sheet Cohort 3Sumitomo PharmaPhase 1/2
39
AGN-151597AbbViePhase 1/2
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CPK850NovartisPhase 1/2
36
Valganciclovir + GanciclovirRochePhase 3
40
ValganciclovirRochePre-clinical
26
Foscarnet sodium + GanciclovirRochePhase 1
29
GanciclovirRochePhase 1
29
GanciclovirRochePre-clinical
26
GanciclovirRochePhase 2
35
GanciclovirRochePre-clinical
26
GanciclovirRochePre-clinical
26
Zidovudine + Sargramostim + GanciclovirRochePre-clinical
26
Zidovudine + GanciclovirRochePre-clinical
26
GanciclovirRochePre-clinical
26
Interferon beta-1b + GanciclovirRochePre-clinical
26
GanciclovirRochePre-clinical
26
GanciclovirRochePre-clinical
26
GanciclovirRochePhase 3
40
ValganciclovirRochePhase 3
36
Cidofovir + ProbenecidGilead SciencesPre-clinical
26