Patisiran

Phase 3Completed
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Interest: 37/100
37
Hype Score

Development Stage

Pre-clinical
Phase 1
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Amyloidosis, Familial

Conditions

Amyloidosis, Familial, Transthyretin Amyloidosis

Trial Timeline

Mar 27, 2019 → Oct 20, 2020

About Patisiran

Patisiran is a phase 3 stage product being developed by Alnylam Pharmaceuticals for Amyloidosis, Familial. The current trial status is completed. This product is registered under clinical trial identifier NCT03862807. Target conditions include Amyloidosis, Familial, Transthyretin Amyloidosis.

What happened to similar drugs?

0 of 11 similar drugs in Amyloidosis, Familial were approved

Approved (0) Terminated (2) Active (9)
🔄NTLA-2001 + PlaceboRegeneron PharmaceuticalsPhase 3
🔄PatisiranAlnylam PharmaceuticalsPhase 3
🔄Nucresiran + Sterile Normal Saline (0.9% NaCl)Alnylam PharmaceuticalsPhase 3
🔄Vutrisiran + Sterile Normal Saline (0.9% NaCl)Alnylam PharmaceuticalsPhase 3
🔄Placebo + PatisiranAlnylam PharmaceuticalsPhase 3
🔄Patisiran + VutrisiranAlnylam PharmaceuticalsPhase 3

Hype Score Breakdown

Clinical
17
Activity
8
Company
12
Novelty
0
Community
0

Clinical Trials (6)

NCT IDPhaseStatus
NCT05505838Pre-clinicalCompleted
NCT05023889Phase 1Active
NCT04201418Pre-clinicalCompleted
NCT03862807Phase 3Completed
NCT02510261Phase 3Completed
NCT01617967Phase 2Completed

Competing Products

20 competing products in Amyloidosis, Familial

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24
Eplontersen Solution for InjectionAstraZenecaPhase 1
29
Treatment of transthyretin (ATTR) amyloidosis in observational study settingAstraZenecaPre-clinical
33
Carfilzomib + DexamethasoneAmgenPhase 1
29
IdelalisibGilead SciencesPhase 2
27
TafamidisPfizerPre-clinical
26
TafamidisPfizerPre-clinical
30
Fx-1006APfizerPhase 2
35
tafamidisPfizerPre-clinical
26
Cyclophosphamide + Dexamethasone + Elotuzumab + LenalidomideBristol Myers SquibbPhase 2
31
IsatuximabBristol Myers SquibbPhase 2
42
Bortezomib + Cyclophosphamide + Dexamethasone + IsatuximabSanofiPhase 1
33
Bendamustine Hydrochloride + IsatuximabSanofiPhase 2
27
NC-503 (Anti-amyloidotic (AA) Agent)GSK plcPhase 2/3
38
NTLA-2001 + PlaceboRegeneron PharmaceuticalsPhase 3
44
LinvoseltamabRegeneron PharmaceuticalsPhase 1/2
39
ALN-TTR01 + Sterile Normal Saline (0.9% NaCl)Alnylam PharmaceuticalsPhase 1
26