Carglumic Acid

Pre-clinicalRecruiting
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Interest: 30/100
30
Hype Score

Development Stage

1
Pre-clinical
2
Phase 1
3
Phase 2
4
Phase 3
5
Approved
Indication / Disease

Methylmalonic Acidemia

Conditions

Methylmalonic Acidemia, Propionic Acidemia

Trial Timeline

Jan 15, 2019 → Jul 30, 2029

About Carglumic Acid

Carglumic Acid is a pre-clinical stage product being developed by Recordati for Methylmalonic Acidemia. The current trial status is recruiting. This product is registered under clinical trial identifier NCT04176523. Target conditions include Methylmalonic Acidemia, Propionic Acidemia.

Hype Score Breakdown

Clinical
3
Activity
15
Company
12
Novelty
0
Community
0

Clinical Trials (2)

NCT IDPhaseStatus
NCT05040178Pre-clinicalRecruiting
NCT04176523Pre-clinicalRecruiting

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4 competing products in Methylmalonic Acidemia

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mRNA-3704ModernaPhase 2
0
mRNA-3705ModernaPhase 2
0