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Timothy (Tim) J. Miller, Ph.D.

Former President, CEO & Co-founder; Strategic Advisor

REGENXBIO

REGENXBIO Pipeline

DrugIndicationPhase
RGX-121Mucopolysaccharidosis Type II (MPS II, Hunter syndrome)Phase I/II/III
RGX-202Duchenne Muscular Dystrophy (DMD)Phase I/II
RGX-381Ocular manifestations of FA (Cone-rod dystrophy)Phase I/II
RGX-314Wet Age-related Macular Degeneration (AMD)Phase II
ABBV-RGX-314Wet Age-related Macular Degeneration (AMD)Phase III