SJ
Therapeutic Areas
GenSight Biologics Pipeline
| Drug | Indication | Phase |
|---|---|---|
| GS010 (Lenadogene Nolparvovec / Lumevoq) | Leber Hereditary Optic Neuropathy (LHON) due to ND4 mutation | Phase 3 |
| GS030 | Retinitis Pigmentosa (RP) | Phase 1/2 |
| Drug | Indication | Phase |
|---|---|---|
| GS010 (Lenadogene Nolparvovec / Lumevoq) | Leber Hereditary Optic Neuropathy (LHON) due to ND4 mutation | Phase 3 |
| GS030 | Retinitis Pigmentosa (RP) | Phase 1/2 |