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Dr. Scott Jeffers

Chief Technical Officer

GenSight Biologics

GenSight Biologics Pipeline

DrugIndicationPhase
GS010 (lenadogene nolparvovec)Leber Hereditary Optic Neuropathy (LHON) due to ND4 mutationPhase 3
GS030Retinitis Pigmentosa (RP)Phase 1/2
Preclinical ProgramsGeographic Atrophy in Dry Age-Related Macular Degeneration (Dry-AMD)Preclinical