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SG

Sarah Gheuens, M.D., Ph.D.

Chief Medical Officer, Head of R&D

Agios Pharmaceuticals

Agios Pharmaceuticals Pipeline

DrugIndicationPhase
Pyrukynd (mitapivat)Hemolytic anemia in adults with Pyruvate Kinase (PK) DeficiencyApproved
MitapivatNon-Transfusion-Dependent ThalassemiaPhase 3
AG-946Hemolytic Anemias and other indicationsPhase 1