MB
Therapeutic Areas
Key2Brain Pipeline
| Drug | Indication | Phase |
|---|---|---|
| TfR-Shuttle Platform | CNS Diseases (enabling technology) | Pre-clinical |
| Chiesi Collaboration (ERT) | Lysosomal Storage Disorders (Neurological) | Pre-clinical |
| OliX Collaboration (siRNA) | Undisclosed CNS Target | Research |