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Laurent Fischer, M.D.

President & Chief Executive Officer, Adverum Biotechnologies

Mirum Pharmaceuticals

Mirum Pharmaceuticals Pipeline

DrugIndicationPhase
LIVMARLI® (maralixibat)Cholestatic pruritus in Alagille syndrome (ALGS)Approved
BrelovitugChronic Hepatitis Delta Virus (HDV)Phase 3
VolixibatCholestatic Liver Diseases (e.g., Primary Sclerosing Cholangitis)Phase 2b/3
Investigational TherapiesCerebrotendinous Xanthomatosis (CTX)Not Specified