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KS

Kapil Saxena, MD, MS

VP, Clinical Development

Metagenomi

Metagenomi Pipeline

DrugIndicationPhase
MGX-001Severe Hypertriglyceridemia (APOC3 Knockout)Preclinical
MGX Platform (CAST)Hemophilia A (Factor VIII Gene Insertion)Preclinical
MGX Platform (Nuclease)Undisclosed CNS TargetPreclinical
MGX Platform (Base Editor)Undisclosed Therapeutic ApplicationPreclinical
MGX Platform (Compact Nuclease)Undisclosed In Vivo ApplicationPreclinical