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JA

Judith A. Dunn, Ph.D.

President of Research and Development

Fulcrum Therapeutics

Fulcrum Therapeutics Pipeline

DrugIndicationPhase
LosmapimodFacioscapulohumeral Muscular Dystrophy (FSHD)Phase 3
Pociredir (FTX-6052)Sickle Cell Disease (SCD)Phase 1b
FTX-6052Beta-thalassemiaDiscovery
FTX-273Diamond Blackfan Anemia / Bone Marrow Failure SyndromesDiscovery