JC

John Crowley

Former CEO, Founding Legacy

Amicus Therapeutics

Amicus Therapeutics Pipeline

DrugIndicationPhase
Galafold (migalastat)Fabry Disease (Pediatric, 2 to <12 yrs)Phase 3
Pombiliti + Opfolda (AT-GAA)Pompe Disease (IOPD, 0 to <18 yrs)Phase 3
DMX-200Focal Segmental Glomerulosclerosis (FSGS)Phase 3
Observational StudyFabry Disease (Women's study)Observational
Observational RegistryFabry Disease (EU)Observational