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Jeannette Potts, Ph.D., J.D.

Chief Legal and Compliance Officer

uniQure

uniQure Pipeline

DrugIndicationPhase
AMT-130Huntington's DiseasePhase 1/2
AMT-162Amyotrophic Lateral Sclerosis (ALS)Preclinical
AMT-260Temporal Lobe Epilepsy / Mesial Temporal Lobe EpilepsyPreclinical
Undisclosed ProgramAlzheimer's DiseasePreclinical
Etranacogene Dezaparvovec (AMT-061)Hemophilia BApproved