Home/Sarepta Therapeutics/Dr. Gilmore O'Neill
DG

Dr. Gilmore O'Neill

EVP, Head of R&D and Chief Medical Officer

Sarepta Therapeutics

Sarepta Therapeutics Pipeline

DrugIndicationPhase
ELEVIDYS (delandistrogene moxeparvovec-rokl)Duchenne Muscular Dystrophy (DMD)Marketed / Phase 3
SRP-5051 (vesleteplirsen)Duchenne Muscular Dystrophy (DMD)Phase 2
SRP-9003Limb-Girdle Muscular Dystrophy Type 2E/R4Phase 3
SRP-6004Myotonic Dystrophy Type 1 (DM1)Phase 1/2
SRP-6005Facioscapulohumeral Muscular Dystrophy (FSHD1)Phase 1/2
EXONDYS 51 (eteplirsen)Duchenne Muscular Dystrophy (DMD)Marketed
VYONDYS 53 (golodirsen)Duchenne Muscular Dystrophy (DMD)Marketed
AMONDYS 45 (casimersen)Duchenne Muscular Dystrophy (DMD)Marketed