EC
Therapeutic Areas
GeneToBe Pipeline
| Drug | Indication | Phase |
|---|---|---|
| Metabolic dysfunction-associated steatohepatitis (siRNA) | MASH | Discovery |
| Alcoholic liver disease (siRNA) | Alcoholic Liver Disease | Discovery |
| Usher syndrome (CRISPR) | Usher Syndrome | Discovery |
| Cystic fibrosis (CRISPR) | Cystic Fibrosis | Discovery |
| Cystic fibrosis (undisclosed) | Cystic Fibrosis | Early Discovery |