AH

Alexander Hardy

President and Chief Executive Officer

BioMarin Pharmaceutical

Roles

President and Chief Executive OfficeratBioMarin Pharmaceutical
President and Chief Executive Officer, BioMarinatVeeva Systems

BioMarin Pharmaceutical Pipeline

DrugIndicationPhase
VOXZOGO (vosoritide)AchondroplasiaCommercial
PALYNZIQ (pegvaliase-pqpz)Phenylketonuria (PKU)Commercial
Enzyme Replacement TherapyMucopolysaccharidosis ICommercial
Gene TherapyHemophilia ACommercial
Metabolic TherapyRare Metabolic ConditionCommercial
ENPP1 deficiency programENPP1 deficiency/GACIClinical