Homology Medicines Pipeline
| Drug | Indication | Phase |
|---|
| HMI-102 | Phenylketonuria (PKU) in adults | Phase 1/2 |
| HMI-103 | Phenylketonuria (PKU) in pediatric patients | Preclinical |
| HMI-203 | Hunter Syndrome (MPS II) | Preclinical |
| HMI-204 | Metachromatic Leukodystrophy (MLD) | Preclinical |