Duchenne Muscular Dystrophy
4 competing products in clinical development for Duchenne Muscular Dystrophy.
Pipeline by Phase
Phase 1/23
Phase 21
All Products (4)
| Product | Company | Stage | Status | Hype |
|---|---|---|---|---|
| DS-5141b | Daiichi Sankyo | Phase 2 | Active | 39 |
| DS-5141b | Daiichi Sankyo | Phase 1/2 | Completed | 32 |
| scAAV9.U7.ACCA | Astellas Pharma | Phase 1/2 | Completed | 32 |
| Phase 1, SQY51 + Phase 2a, SQY51 (cohort 1) + Phase 2a, SQY51 (cohort 2) + Phase 2a, SQY51 (cohort 3) | Biotrial | Phase 1/2 | Recruiting | 29 |