Zilganersen (ION373)
Alexander Disease (AxD)
NDA SubmittedPriority Review
Key Facts
Indication
Alexander Disease (AxD)
Phase
NDA Submitted
Status
Priority Review
Company
About Ionis Pharmaceuticals
Ionis Pharmaceuticals is a commercial-stage biotech leader with a mission to discover and deliver life-changing RNA-targeted medicines. The company has achieved multiple industry firsts, including the first approved antisense drug, and has successfully transitioned from a research-focused entity to a fully integrated organization with its own commercial capabilities. Its strategy centers on independently launching medicines in neurology and cardiology while selectively partnering in other areas, backed by a deep, late-stage pipeline and a sustainable technology platform.
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