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Undisclosed In Vivo Program

Sickle Cell Disease (SCD) / Beta thalassemia

ResearchActive

Key Facts

Indication
Sickle Cell Disease (SCD) / Beta thalassemia
Phase
Research
Status
Active
Company

About Editas Medicine

Editas Medicine is a clinical-stage leader in CRISPR-based gene editing, founded in 2013 and headquartered in Cambridge, Massachusetts. The company's strategy centers on developing in vivo gene editing medicines, with its most advanced program, EDIT-401 for hyperlipidemia, poised for human proof-of-concept by end of 2026. While facing a competitive landscape and significant clinical and financial risks, Editas possesses foundational IP and a differentiated platform that could yield best-in-class, potentially curative therapies.

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