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TransCon CNP (navepegritide)

Achondroplasia (infants aged 0–2)

Pivotal Phase 2Active, RecruitingNCT06079398

Key Facts

Indication
Achondroplasia (infants aged 0–2)
Phase
Pivotal Phase 2
Status
Active, Recruiting
Company

About Ascendis Pharma

Ascendis Pharma is a mission-driven biotech focused on developing novel therapeutics for rare endocrine diseases and oncology using its proprietary TransCon (transient conjugation) platform. The company has achieved commercial success with its first product, Skytrofa (TransCon hGH), and is advancing a deep pipeline, including late-stage candidates for achondroplasia and hypoparathyroidism. Its strategy combines internal development with strategic geographic partnerships to maximize the global potential of its platform, aiming to build a leading, fully integrated biopharmaceutical company.

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