ST-503
Small Fiber Neuropathy (SFN)
Key Facts
About Sangamo Therapeutics
Sangamo Therapeutics is a genomic medicine company with a mission to develop lasting, potentially curative therapies for severe diseases using its foundational zinc finger protein (ZFP) technology. The company has achieved clinical proof-of-concept across multiple modalities, most notably with its lead gene therapy candidate, isaralgagene civaparvovec (ST-920), for Fabry disease, for which it is preparing a Biologics License Application (BLA) submission. Its strategy combines advancing a wholly-owned neurology pipeline with leveraging its platform through strategic collaborations with major pharmaceutical firms like Pfizer, Novartis, Takeda, and Lilly to expand into other therapeutic areas and share development costs.
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