Home/Pipeline/Setmelanotide

Setmelanotide

Prader-Willi syndrome

Phase 3Active

Key Facts

Indication
Prader-Willi syndrome
Phase
Phase 3
Status
Active
Company

About Rhythm Pharmaceuticals

Rhythm Pharmaceuticals specializes in developing precision medicines for rare diseases of obesity and metabolic dysfunction caused by genetic deficiencies in the melanocortin-4 (MC4) pathway. Their flagship product IMCIVREE represents the first FDA-approved therapy specifically for certain rare genetic obesities, addressing significant unmet medical needs. The company continues to expand the clinical utility of setmelanotide across additional rare obesity syndromes while building a robust pipeline of next-generation therapies.

View full company profile

About Rhythm Pharmaceuticals

Rhythm Pharmaceuticals specializes in developing precision medicines for rare diseases of obesity and metabolic dysfunction caused by genetic deficiencies in the melanocortin-4 (MC4) pathway. Their flagship product IMCIVREE represents the first FDA-approved therapy specifically for certain rare genetic obesities, addressing significant unmet medical needs. The company continues to expand the clinical utility of setmelanotide across additional rare obesity syndromes while building a robust pipeline of next-generation therapies.

View full company profile

About Rhythm Pharmaceuticals

Rhythm Pharmaceuticals specializes in developing precision medicines for rare diseases of obesity and metabolic dysfunction caused by genetic deficiencies in the melanocortin-4 (MC4) pathway. Their flagship product IMCIVREE represents the first FDA-approved therapy specifically for certain rare genetic obesities, addressing significant unmet medical needs. The company continues to expand the clinical utility of setmelanotide across additional rare obesity syndromes while building a robust pipeline of next-generation therapies.

View full company profile

Other Prader-Willi syndrome Drugs

DrugCompanyPhase
ACP-101 (intranasal carbetocin)Acadia PharmaceuticalsPhase 2/3
NNZ-2591Neuren PharmaceuticalsPhase 2