RP-L102
Fanconi Anemia (FA) Complementation Group A
Phase 2Active (referenced on site)
Key Facts
Indication
Fanconi Anemia (FA) Complementation Group A
Phase
Phase 2
Status
Active (referenced on site)
Company
About Rocket Pharmaceuticals
Rocket Pharmaceuticals is a publicly traded gene therapy company dedicated to developing curative treatments for rare genetic disorders. Its most advanced program targets Danon Disease, a life-threatening cardiac condition, with a Phase 2 pivotal trial underway. The company leverages its expertise in gene therapy platforms to build a pipeline addressing significant unmet medical needs, guided by a patient-centric philosophy and core values of trust, generosity, curiosity, and elevation.
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