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PAX-101 (IV Suramin)

Autism Spectrum Disorder (ASD)

Phase 3Completed (Topline Results Announced 2024)

Key Facts

Indication
Autism Spectrum Disorder (ASD)
Phase
Phase 3
Status
Completed (Topline Results Announced 2024)
Company

About PaxMedica

PaxMedica is a focused, clinical-stage biotech advancing PAX-101, an intravenous formulation of the century-old drug suramin, for neurological disorders. The company's strategy is based on the hypothesis that modulating the purinergic signaling pathway can treat core symptoms of Autism Spectrum Disorder (ASD) and Fragile X-associated Tremor/Ataxia Syndrome (FXTAS). Key achievements include completing a Phase 3 trial in ASD and securing Orphan Drug Designation for PAX-101 in FXTAS. Its path forward is defined by advancing its concentrated pipeline through regulatory milestones while navigating the high-risk, high-reward landscape of CNS drug development.

View full company profile

About PaxMedica

PaxMedica is a focused, clinical-stage biotech advancing PAX-101, an intravenous formulation of the century-old drug suramin, for neurological disorders. The company's strategy is based on the hypothesis that modulating the purinergic signaling pathway can treat core symptoms of Autism Spectrum Disorder (ASD) and Fragile X-associated Tremor/Ataxia Syndrome (FXTAS). Key achievements include completing a Phase 3 trial in ASD and securing Orphan Drug Designation for PAX-101 in FXTAS. Its path forward is defined by advancing its concentrated pipeline through regulatory milestones while navigating the high-risk, high-reward landscape of CNS drug development.

View full company profile

About PaxMedica

PaxMedica is a focused, clinical-stage biotech advancing PAX-101, an intravenous formulation of the century-old drug suramin, for neurological disorders. The company's strategy is based on the hypothesis that modulating the purinergic signaling pathway can treat core symptoms of Autism Spectrum Disorder (ASD) and Fragile X-associated Tremor/Ataxia Syndrome (FXTAS). Key achievements include completing a Phase 3 trial in ASD and securing Orphan Drug Designation for PAX-101 in FXTAS. Its path forward is defined by advancing its concentrated pipeline through regulatory milestones while navigating the high-risk, high-reward landscape of CNS drug development.

View full company profile

Other Autism Spectrum Disorder (ASD) Drugs

DrugCompanyPhase
SCI-210SciSparcPhase II
eTNS PlatformNeuroSigmaUnknown
CM-ATCuremarkPhase 3
DT402Definium TherapeuticsPhase 2a
ML-004MapLight TherapeuticsPhase 1