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Neuromuscular Program

Late-onset Pompe disease

PreclinicalActive

Key Facts

Indication
Late-onset Pompe disease
Phase
Preclinical
Status
Active
Company

About Creyon Bio

Creyon Bio is a private, pre-clinical biotech company pioneering a novel approach to RNA drug delivery using aptamers and artificial intelligence. Its core technology platform aims to overcome key limitations of traditional antibody-based delivery and lipid nanoparticles by enabling precise, cell-specific targeting of therapeutic payloads like siRNA and ASOs. The company has established preclinical proof-of-concept in three therapeutic areas—immunology, CNS, and neuromuscular diseases—and is advancing a wholly-owned pipeline. Creyon represents a convergence of next-generation delivery science and computational drug design, positioning it to develop potentially safer and more effective RNA therapies.

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Other Late-onset Pompe disease Drugs

DrugCompanyPhase
AT845 (FORCE)astellasPhase 1/2
AT845Astellas PharmaPhase 1/2