JLK-247

About Phoenix Nest

Phoenix Nest is a private, pre-revenue biotech pioneering therapies for Sanfilippo syndrome, a fatal pediatric neurodegenerative disorder. Its pipeline includes gene therapy, enzyme replacement, and a neuroprotective peptide program, all supported by over $17 million in non-dilutive grants from the NIH and patient foundations. The company is characterized by a patient-founder ethos, a strong academic partnership network, and programs advancing through preclinical and early clinical study stages. Its mission is driven by an inherent sense of urgency to address these unmet medical needs.

Therapeutic Areas