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IB1001 (N-acetyl-L-leucine)

Niemann-Pick disease type C (NPC)

Phase 3Active

Key Facts

Indication
Niemann-Pick disease type C (NPC)
Phase
Phase 3
Status
Active
Company

About IntraBio

IntraBio is a clinical-stage biotech developing IB1001 (N-acetyl-L-leucine), an oral modified amino acid, for rare neurological disorders. Its lead program for Niemann-Pick disease type C (NPC) has reported positive Phase III results, and the company has achieved its first FDA approval with AQNEURSA™ (levacetylleucine) for an undisclosed indication. The company leverages a scientific foundation from key academic institutions and is advancing a pipeline targeting common neurological disorders and healthspan.

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