Helex‑ADPKD‑1
Autosomal Dominant Polycystic Kidney Disease (PKD1 mutation)
PreclinicalActive
Key Facts
Indication
Autosomal Dominant Polycystic Kidney Disease (PKD1 mutation)
Phase
Preclinical
Status
Active
Company
About Helex Bio
Helex Bio builds kidney‑targeted, non‑viral gene‑editing therapies using lipid nanoparticles and AI‑driven drug design.
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