Giroctocogene fitelparvovec (SB-525)
Hemophilia A
Phase 3Active, Not Recruiting
Key Facts
About Sangamo Therapeutics
Sangamo Therapeutics is a genomic medicine company with a mission to develop lasting, potentially curative therapies for severe diseases using its foundational zinc finger protein (ZFP) technology. The company has achieved clinical proof-of-concept across multiple modalities, most notably with its lead gene therapy candidate, isaralgagene civaparvovec (ST-920), for Fabry disease, for which it is preparing a Biologics License Application (BLA) submission. Its strategy combines advancing a wholly-owned neurology pipeline with leveraging its platform through strategic collaborations with major pharmaceutical firms like Pfizer, Novartis, Takeda, and Lilly to expand into other therapeutic areas and share development costs.
View full company profileTherapeutic Areas
Other Hemophilia A Drugs
| Drug | Company | Phase |
|---|---|---|
| GS1191 | Gritgen Therapeutics | Phase 1 |
| FVIII-GMAC | CellGenTech | Preclinical |
| BIVV001 (rFVIIIFc-VWF-XTEN) | Swedish Orphan Biovitrum | Phase 3 |
| Coagulation Factor VIII | Shanghai RAAS Blood Products | Marketed |
| Human Coagulation Factor VIII | Hualan Biological Engineering | Marketed |