Friedreich's Ataxia Program
Friedreich's Ataxia
PreclinicalActive
Key Facts
About StrideBio
StrideBio, founded in 2015 and based in Durham, NC, is a private, pre-revenue biotech focused on advancing gene therapy through its novel AAV engineering platform. The company's STRIVE platform utilizes structure-inspired design to create capsids with improved tropism, reduced pre-existing immunity, and enhanced manufacturability compared to natural AAV serotypes. Its lead programs target genetic conditions like Friedreich's ataxia and a severe pediatric epilepsy (SLC13A5 deficiency), with a broader pipeline in discovery and preclinical stages. StrideBio has secured significant venture funding and established key partnerships with Takeda and Arbor Biotechnologies to validate and expand its platform's reach.
View full company profileTherapeutic Areas
Other Friedreich's Ataxia Drugs
| Drug | Company | Phase |
|---|---|---|
| Gene therapy for Friedreich's ataxia | Biointaxis | Pre-clinical |
| Nomlabofusp (CTI-1601) | Larimar Therapeutics | Phase 2 |