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FLT201

Type 1 Gaucher Disease

Phase 1/2Active

Key Facts

Indication
Type 1 Gaucher Disease
Phase
Phase 1/2
Status
Active
Company

About Spur Therapeutics

Spur Therapeutics is a UK-based, clinical-stage biotech pioneering optimized gene therapies. Its lead candidate, FLT201, is an AAV gene therapy for Type 1 Gaucher disease, with promising two-year Phase 1/2 data presented in 2026. The company's strategy involves leveraging its platform to expand from rare diseases into larger indications like Parkinson's, dementia, and cardiovascular conditions, aiming for transformational, one-time treatments.

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