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FALCON Study (implied program)

Primary Mitochondrial Disease

Phase 2/3Active

Key Facts

Indication
Primary Mitochondrial Disease
Phase
Phase 2/3
Status
Active
Company

About Abliva

Abliva is a clinical-stage biotech company dedicated to addressing the high unmet medical need in primary mitochondrial diseases, a rare and severe orphan condition affecting an estimated 1 in 5,000 people. The company leverages in-house R&D capabilities to build a portfolio of small molecule projects with mechanisms of action suitable for a range of mitochondrial disorders, with programs spanning from early discovery to clinical phases. Its acquisition by Pharming Group in mid-2025 provides a strategic parent with resources and commercial expertise in rare diseases, potentially accelerating the development and future commercialization of Abliva's pipeline.

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