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ENTR-601-50

Duchenne Muscular Dystrophy (Exon 50 skipping)

PreclinicalActive

Key Facts

Indication
Duchenne Muscular Dystrophy (Exon 50 skipping)
Phase
Preclinical
Status
Active
Company

About Entrada Therapeutics

Entrada Therapeutics is a clinical-stage biotechnology company with a mission to overcome the fundamental challenge of intracellular drug delivery. Its core innovation is the Endosomal Escape Vehicle (EEV) platform, a versatile technology enabling the efficient delivery of therapeutic molecules into the cell cytoplasm. The company is advancing a pipeline of oligonucleotide-based candidates for serious genetic neuromuscular disorders, with its lead program, ENTR-601-44 for DMD exon 44 skipping, in Phase 1/2b trials. Entrada's strategy leverages its platform to target high-unmet-need diseases with validated biology but historically inaccessible targets.

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