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DX5057

Facioscapulohumeral Muscular Dystrophy (FSHD)

PreclinicalIND-Enabling studies planned for 2025

Key Facts

Indication
Facioscapulohumeral Muscular Dystrophy (FSHD)
Phase
Preclinical
Status
IND-Enabling studies planned for 2025
Company

About Altay Therapeutics

Altay Therapeutics is a private, preclinical-stage biotech focused on unlocking transcription factors as therapeutic targets. The company's core technology is a therapeutic area-agnostic platform that identifies novel allosteric sites on transcription factors to design highly selective oral inhibitors. With its lead FSHD program expected to enter IND-enabling studies in 2025 and a STAT3 inhibitor in lead optimization, Altay is positioning itself as a leader in a challenging but high-potential drug discovery space, supported by grants and recognition from major pharmaceutical companies.

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Other Facioscapulohumeral Muscular Dystrophy (FSHD) Drugs

DrugCompanyPhase
AOC ProgramAvidity BiosciencesClinical
DYNE-301Dyne TherapeuticsPhase 1/2
Losmapimod (FHD-286)Fulcrum TherapeuticsPhase 3