AVP-6

Sanfilippo syndrome (MPS III A-D) - Neuroprotection

DiscoveryActive

Key Facts

Indication
Sanfilippo syndrome (MPS III A-D) - Neuroprotection
Phase
Discovery
Status
Active
Company

About Phoenix Nest

Phoenix Nest is a private, pre-revenue biotech pioneering therapies for Sanfilippo syndrome, a fatal pediatric neurodegenerative disorder. Its pipeline includes gene therapy, enzyme replacement, and a neuroprotective peptide program, all supported by over $17 million in non-dilutive grants from the NIH and patient foundations. The company is characterized by a patient-founder ethos, a strong academic partnership network, and programs advancing through preclinical and early clinical study stages. Its mission is driven by an inherent sense of urgency to address these unmet medical needs.

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